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【多倫多病童醫院再顯神通 】為患罕有病男童進行全球首項治療
(2022/8/15)
【明報專訊】多倫多一名男童因為基因錯亂患上罕有的疫病spastic paraplegia 5 (SPG50),令致身體發育受阻。
他現受多倫多病童醫院全國首項的基因改造治療。
男童家人多年來籌款,合共籌得三百多萬元,將會用作全球罕有的80名SPG50患者。
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